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Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

2011

Cirak, Sebahattin | Arechavala-Gomeza, Virginia | Guglieri, Michela | Feng, Lucy | Torelli, Silvia | Anthony, Karen | Abbs, Stephen | Garralda, Maria Elena | Bourke, John | Wells, Dominic J | Dickson, George | Wood, Matthew JA | Wilton, Steve D. | Straub, Volker | Kole, Ryszard | Shrewsbury, Stephen B. | Sewry, Caroline | Morgan, Jennifer E | Bushby, Kate | Muntoni, Francesco


Библиографическая информация
lancet
Том 378 Выпуск 9791 Нумерация страниц 595 - 605 ISSN 0140-6736
Издатель
Elsevier Ltd.
Другие темы
Neuronal nitric oxide synthase; Boys; Reverse transcriptase polymerase chain reaction; Dystrophin; Biomedical research
Язык
Английский
Тип
Journal Article; Text

2024-02-28
MODS
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